“We often assume we know what is the most debilitating aspect of a disease, while patients might have a different direct experience.”
Gene therapies are progressing at a rapid pace, meaning that it is difficult to stand back and assess the real challenges facing this field as well as future opportunities. That’s why we have conducted an industry-wide survey, gathering together the thoughts and opinions of experts working to address the unmet need in the rare disease space with gene therapies. Here are the results!
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