Pre Conference Workshop Day

Gene Therapy 101 Day |A Full Day Workshop Session | 9.00AM - 4.00PM

The accelerated recent development of the gene therapy space brings with it drug developers rapidly recruiting to grow their gene therapy program teams. Specifically designed for new entrants to the field, our full-day 101 workshop will offer a streamlined mixture of plenaries and interactive learning experiences, delivered by gene therapy industry leaders. Co-designed with our workshop leaders, the workshop will address the unique challenges encountered when working with gene therapies, including:

Viral vectors for gene therapies in a nutshell: an overview of current approaches, their relevant merits, and drawbacks

Gregory Stewart, Executive Consultant, Alcyone Life Sciences

Developing key safety and efficacy endpoints for rare gene therapy clinical trials
Bert Yao, Vice President Clinical Development, PTC Therapeutics

Overcoming the challenges associated with scaling-up to commercial manufacturing

Kumar Dhanasekharan, Senior Vice President, Technical Operations, Renovacor

Understanding the intricacies of patient recruitment and enrolment

Jessica Riviere, Vice President Patient Advocacy & Patient Engagement, Ultragenyx

Translating basic research programs into the clinic and beyond

Giri Murlidharan, Director - Translational Science Affinia Therapeutics

The keys to success with regulatory filings and interactions
Jim Wang, Chief Regulatory Officer Adverum Biotechnologies

This workshop will cover key elements, including:

101 DAY

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