Clinical Case Study: Executing a Gene Therapy Trial in New Geographies: The Experience with The OAV101 IT Trial In Later Onset Spinal Muscular Atrophy
Time: 1:30 pm
day: Day 2- Clinical 2
Details:
• Insights into adapting clinical trial protocols and overcoming logistical challenges in diverse regulatory environments for gene therapy trials
• Key takeaways from conducting the OAV101 IT trial for later-onset spinal muscular atrophy in varied international settings
• Strategies to maintain data integrity, patient safety, and regulatory alignment across multiple geographic regions
