Industry Leaders Panel: Accelerating Gene Therapies for Rare Disease Patients – Where are the Bottlenecks & How Can we Overcome Them?

Time: 9:30 am
day: Day One


Gene therapy continues to make significant progress with no signs of slowing down, but the past year has also flagged distinct development challenges that need to be overcome. This panel discussion will bring together experts from pioneering gene therapy companies leading the way to pinpoint these obstacles and explore how we can address them to bring gene therapies to patients more quickly, safely, and effectively:

  • How are manufacturing processes evolving to meet regulatory benchmarks?
  • Adapting to the novelty of gene therapies with respect to regulatory, pricing, market access, and patient needs
  • Accelerating gene therapy programs while maintaining safety and quality standards
  • Leading by example: how the leading companies are paving the way for the future of gene therapy