Virtual: Rare Disease Gene Therapy Development: Where Has It Been and Where Is It Going?

Time: 8:30 am
day: Day One

Details:

  • Comparing progress in rare disorders in vivo with developments seen in CAR-T and ex vivo cell modified gene therapies
  • Where are the current bottlenecks for gene therapy approvals?
  • Addressing FDA’s outlook for gene therapy in 2022

Speakers: