Welcome to the 8th Gene Therapy Development Summit
Transforming the Future of Gene Therapies for Rare & Common Diseases
With 14 new gene therapy approvals in the last 18 months, billion-dollar collaborations, and the development of treatments for more common conditions, the gene therapy field is rapidly gaining momentum and broadening scope beyond rare diseases. Returning to Boston in March, the 8th Gene Therapy Development Summit, formerly known as the Gene Therapy for Rare Disorders Summit, will unite 200+ gene therapy experts to tackle the field’s biggest challenges of achieving genuine scalability and accessibility to meet growing patient demand.
For the first time, this industry-defining meeting will reflect the field’s growing focus on developing therapies for common diseases, whilst addressing existing hurdles in rare and ultra-rare disorders. This is your unparalleled opportunity to delve into:
The latest global regulatory requirements
Optimizing routes for CNS
Ocular and inner ear disorders
Innovations in capsid engineering and dosing strategies
Increasing volumetric productivity to reduce CoGs
Join your peers to drive gene therapy innovation across translational, clinical, regulatory, and manufacturing tracks. This event is designed to help attendees navigate the entire gene therapy pipeline.
By refining gene delivery platforms, optimizing manufacturing processes, and navigating regulatory pathways, we can revolutionize the future of gene therapies—bringing them to broader patient populations and significantly enhancing clinical outcomes.