Welcome to the 8th Gene Therapy Development Summit
Transforming the Future of Gene Therapies for Rare & Common Diseases
The Gene Therapy Development Summit, formerly known as the Gene Therapy Rare Disorders Summit, now reflects the field’s broader scope beyond rare diseases. This evolution mirrors the growing focus on developing therapies that address common diseases, while still tackling existing challenges in rare and ultra-rare disorders.
The summit returns as the go-to-meeting by providing an unparalleled opportunity to delve into:
The latest global regulatory requirements
Optimizing routes for CNS
Ocular and inner ear disorders
Innovations in capsid engineering and dosing strategies
Increasing volumetric productivity to reduce CoGs
Join your peers to drive gene therapy innovation across translational, clinical, regulatory, and manufacturing tracks. This event is designed to help attendees navigate the entire gene therapy pipeline.
By refining gene delivery platforms, optimizing manufacturing processes, and navigating regulatory pathways, we can revolutionize the future of gene therapies—bringing them to broader patient populations and significantly enhancing clinical outcomes.
World-Class Speaker Faculty Includes:
Previously Attending Companies Include:
Our Partners:
Other Events In The Gene Therapy Series
