Gene Therapy for Rare Disorders is dedicated to overcoming the unique drug development challenges encountered in transforming gene therapy concepts into reality for rare disease patients in need.

As the gene therapy field strives to strike the balance between clinical efficacy and product safety in the context of mounting regulatory scrutiny, Gene Therapy for Rare Disorders 2022 will provide in-depth insights from experts who know how to drive clinical progress, optimize manufacturing, and demonstrate the value of gene therapy products to regulators, payers, and patients.

Across four days, this meeting will unite 600+ leading experts in Boston from innovative biotechs, large pharma, academia, and key service provider companies, delivering actionable insights and valuable networking opportunities to accelerate gene therapy progress.

This is your comprehensive guide to define your commercial path forward.

Health & Safety

The health, safety and well-being of our community remains our highest priority. Therefore, all attendees will be required to complete a health declaration prior to attending the event. As part of this, attendees must declare that they are either fully vaccinated and /or have completed a negative Lateral Flow Test or PCR Test within 48 hours the event*.

For further information around Health and Safety onsite, please visit our FAQ here.

*Please note, this is subject to change at any time without prior notice.

What You Can Expect at Gene Therapy For Rare Disorders 2022:

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Lead Partner:

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Expertise Partners:

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Azzur
Andelyn
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charles river

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