The 4th Annual Gene Therapy for Rare Disorders will focus exclusively on overcoming the late-stage commercial challenges drug developers face when delivering gene therapies to market.

With approvals in a number of indications over the last year, and more rapidly approaching on the horizon, the meeting will leverage the experience from first to market pioneers, as well as unveiling the strategies
drug developers are employing to improve efficacy, safety and commercial viability.

Incorporating insights from 80+ industry-leading speakers, this conference will delve into the key regulatory, reimbursement, clinical and manufacturing hurdles that need to be overcome to realize the commercial potential of gene therapies.

Join 600+ of your colleagues to accelerate the progress of the next generation of gene therapies.

This is your comprehensive guide to define your commercial path forward.


Access the official agenda to see the topics that will be addressed.

World-Class Speaking Faculty

Pamela Bradt



Katherine Dallow

VP, Clinical Programs & Strategy

Blue Cross Blue Shield of Massachusetts

Kei Kishimoto


Selecta Biosciences

Luis Maranga


Voyager Therapeutics

Peter Marks

Director, CBER


Chris Mason



Emily McGinnis

VP, Patient Advocacy & Professional Relations


Federico Mingozzi


Spark Therapeutics

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