Gene Therapy for Rare Disorders is dedicated to overcoming the unique drug development challenges encountered in transforming gene therapy concepts into reality for rare disease patients in need.

As the gene therapy field strives to strike the balance between clinical efficacy and product safety in the context of mounting regulatory scrutiny, Gene Therapy for Rare Disorders provides in-depth insights from experts who know how to drive clinical progress, optimize manufacturing, and demonstrate the value of gene therapy products to regulators, payers, and patients.

Across four days, this meeting will unite 500+ leading experts in Boston from innovative biotechs, large pharma, academia, and key service provider companies, delivering actionable insights and valuable networking opportunities to accelerate gene therapy progress.

This is your comprehensive guide to define your commercial path forward.

View the 2022 event guide to see what you missed.

‘The conference was very well attended and very informative to a wider industry audience; not just manufacturing, but clinical and commercialization as well.’

Vertex Pharmaceuticals - 2022 Attendee

With Thanks To Our Lead Partner:

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Expertise Partners Included:

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‘Outstanding networking. Pleasure to find opportunities for cross functional learning amongst peers.
High quality speakers, outstanding job.’

Neurogene - 2022 Attendee

Other Events In The Gene Therapy Series: