Overcome Clinical, Manufacturing, Regulatory & Commercial Challenges from Clinical Trial Initiation Through to Approval and Turn the Significant Potential of Gene Therapies into a Commercial Reality

Thank you to our speakers, sponsors, and delegates who joined us in Boston for the summit! If you are interested in the 2025 event, please get in touch at info@hansonwade.com

What You Missed in 2024:

This past year has seen more gene therapies approved by the FDA than the previous five years combined, and almost triple the number of clinical trials in gene therapy have been initiated in H1 of 2023 compared to the same time frame in the previous year. 

To maximize the value of your late-stage gene therapy assets, the 7th Gene Therapy for Rare Disorders Summit returned to tackle head-on the significant clinical, manufacturing, regulatory, and commercial challenges facing gene therapy programs. 

Bringing together key figures from industry, regulatory bodies, patient non-profits, payers, and key service providers, this was the field’s foremost meeting for collectively progressing rare gene therapy programs into and through the clinic.  

We joined together over 200 peers from leading biopharma companies with direct experience in driving gene therapies through the clinic and into the market.

3

DEEP DIVE

TRACKS

9

ADDITIONAL WORKSHOPS &

FOCUS DAYS

70+

EXPERT SPEAKERS

SHARING INSIGHTS

100+

COMPANIES

REPRESENTED

200+

ATTENDEES TO

NETWORK WITH

The Expert Speaker Faculty Included:

Liz Fowler

Director, CMS Innovation Center

Centers for Medicare & Medicaid Services

Michael Sherman

Venture Partner

RA Capital Management

Monica Hayhurst Bennett

Head of Gene Therapy Unit, Neuroscience

Novartis

Pat Furlong

Founding President & Chief Executive Officer

Parent Project Muscular Dystrophy

Peter Marks

Director

FDA

Richard Colvin

Chief Medical Officer

bluebird bio

Sheila Mikhail

Co-Founder & Former Chief Executive Officer

AskBio

Tim Hunt

Chief Executive Officer

Alliance for Regenerative Medicine

GTx Rare 2
GTx 5
GTx Rare 1

Lead Partner:

precision for medicine

Expertise Partner:

azzur_group

Program Partners:

AGC Biologics
advancedmedicinepartners_logo
Matica Logo
VintaBio Logo 400 x 400 copy

Hosting Partner:

Worldwide Clinical Trials logo

Exhibition Partners:

Forge Biologics Logo
cryoport systems - logo
Kyfora_Logo_Primary_TaglineLocku
Paysign_Primary Logo_4C_CMYK
sgs

Program Partners:

AGC Biologics
Matica Logo
VintaBio Logo 400 x 400 copy
advancedmedicinepartners_logo

Expertise Partner:

Hosting Partner:

azzur_group
Worldwide Clinical Trials logo

Exhibition Partners:

Forge Biologics Logo
cryoport systems - logo
Kyfora_Logo_Primary_TaglineLocku
Paysign_Primary Logo_4C_CMYK
sgs

Event Partners:

bostonbiodevelopment_logo
compliance architects

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