Decentralized Development of Gene Therapies for Ultra-Rare Disorders

Time: 4:15 pm
day: Day One PM

Details:

  • Realizing the full value potential for investing into Gene Therapies for Ultra-Rare Disorders
  • Strategies and tools for decentralized funding of low-cost CMC platforms for viral vectored Gene Therapies
  • Lowering the patient prevalence threshold for financial sustainability through greater industry collaboration

Speakers: