Effective Strategies for Transitioning from Rare to Common Diseases to Expand Gene Therapy Horizons
Time: 9:30 am
day: Focus Day
Details:
• Analysis of the challenges and opportunities in scaling gene therapy technologies from rare to common diseases, including adjustments in clinical trial design and patient populations
• Examination of strategies to reduce production costs and enhance cost-effectiveness while maintaining high-quality standards for larger patient populations
• Insights into the regulatory hurdles and market strategies required to successfully transition therapies to broader indications and achieve widespread adoption
