Panel Discussion: Reaching, Enrolling, and Retaining Participants in Rare Disease Gene Therapy Trials

Time: 2:00 pm
day: Clinical - PM


  • Multi-stakeholder discussion of friction points in the development lifecycle and how to overcome them: what have we tried, what has been successful and under what circumstances
  • Dissection of real-world examples over time and across different patient communities
  • Analysis of recent trends and impacts of continuing advances