Panel Discussion: Unpicking the Complexities of External Control Arms

Time: 12:00 pm
day: Clinical - AM

Details:

• Identifying the challenges associated with conducting robust external control arm studies in small, heterogenous patient cohort
• Methodological considerations for using external control arms to credibly demonstrate the effectiveness of a rare gene therapy
• Key lessons learned from clinical trial designs incorporating external controls
• Considerations for using natural history studies as external control arms

Speakers:

Monica Hayhurst Bennett Monica Hayhurst Bennett is a Director leading the Gene Therapy Unit in the Neuroscience Disease Area of the Novartis Biomedical Research, where she is responsible Read more

Daniel Chung Dr. Chung is a trained ophthalmologist who has been instrumental in the development of genetic ocular therapies for blinding diseases for almost 30 years, in Read more

Heather Lau Dr. Lau is executive director of Global Clinical Development at Ultragenyx and is a board-certified neurologist with special qualifications in pediatrics. Prior to joining industry Read more