Mitra Tavakkoli
Executive Medical Lead BridgeBio Pharma, Inc.
Seminars
Thursday 26th March 2026
Panel Discussion: Connecting with Communities to Build Trust in Clinical Research
4:30 pm
- Building trust through transparent education that supports long-term trial participation
- Translating complex gene therapy concepts into clear, accessible materials for families and caregivers
- Sharing real-world strategies that improve recruitment, retention, and patient satisfaction
Thursday 26th March 2026
Navigating Placebo Control Arms in Rare Disease Clinical Trials
5:15 pm
- Weighing the pros and cons of placebo versus historical controls in small patient populations
- Understanding evolving regulatory guidance and recent approvals granted without control arms
- Addressing competitive pressures and leveraging shared natural history studies to strengthen trial design
