Van Hoang

Company: Spark Therapeutics

Job title: Head of Analytical & Quality Control

Seminars:

CMC Strategies to Scale Gene Therapy for Common Diseases: A Roadmap to Quality and Efficiency 11:00 am

• Process Innovation for High-Volume Production: Leveraging modular production and advanced technologies to meet the demands of large-scale gene therapy applications in common diseases • Building a Quality-Driven Manufacturing Framework: Establishing robust analytics, in-process controls, and release testing to ensure product consistency at scale • Integrating Cost-Effective CMC Solutions: Developing strategies for streamlined process validation,…Read more

day: Focus Day

Panel Discussion: Breaking Boundaries: Navigating the Shift from Rare to Common Diseases in Gene Therapy 1:30 pm

• Exploring the unique challenges and benefits of expanding gene therapy into more prevalent conditions, including patient access, cost, and treatment scalability • Evaluating the feasibility of widespread gene therapy applications in common diseases by 2025, along with realistic goals and potential hurdles • Essential factors for successful translation, including regulatory preparedness, CMC adaptation, and…Read more

day: Focus Day