Van Hoang
Company: Spark Therapeutics
Job title: SVP, Head of Analytical & Quality Control
Seminars:
CMC Strategies to Scale Gene Therapy for Common Diseases: A Roadmap to Quality and Efficiency 11:00 am
• Process Innovation for High-Volume Production: Leveraging modular production and advanced technologies to meet the demands of large-scale gene therapy applications in common diseases • Building a Quality-Driven Manufacturing Framework: Establishing robust analytics, in-process controls, and release testing to ensure product consistency at scale • Integrating Cost-Effective CMC Solutions: Developing strategies for streamlined process validation,…Read more
day: Focus Day
Panel Discussion: Breaking Boundaries: Navigating the Shift from Rare to Common Diseases in Gene Therapy 1:30 pm
• Exploring the unique challenges and benefits of expanding gene therapy into more prevalent conditions, including patient access, cost, and treatment scalability • Evaluating the feasibility of widespread gene therapy applications in common diseases by 2025, along with realistic goals and potential hurdles • Essential factors for successful translation, including regulatory preparedness, CMC adaptation, and…Read more
day: Focus Day