Speakers Included

Ales Strancar

Managing Director

BIA Separations, Part of Sartorius Group

Deborah Ascheim

CMO

StrideBio

Jonathan Rush

Head of Supply Chain and Operational Excellence

Andelyn Biosciences

Ravi Samavedam

Chief Innovation Officer (CINO)

Azzur Group

Barbara Bonamassa ‘To be confirmed’

Quality Assessor

AIFA ‘To be confirmed’

Eduard Ayuso

CTO

DiNAQOR

Luca Biasco

Senior Director, Translational Research

AVROBIO

Luigi Barbarossa

Senior Research Associate

AVROBIO

Christa Feasley, Ph.D.

Senior Analytical Development Scientist

Cytovance

Mike Byrne

Senior Director, Analytical Development & Product Quality

REGENXBIO

Ruth Castellanos

Associate Director

Stridebio

Ying Cai

Senior Director, Process Development

Ultragenyx

Daniel Chung

CMO

SparingVision

Fernanda Copeland

Executive Director, Global Head of Patient Advocacy & Engagement

AVROBIO

Kent Christopherson

Senior Director, Medical Affairs

Orchard Therapeutics

Nancy Yu

Co-Founder & CEO

All Stripes Research

Eric Faulkner

VP, Global RWE

Novartis Gene Therapies

Rebecca Derwin

Director, Early Commercial Strategy, Rare Programs

REGENXBIO

Scott Dorfman

CEO

Odylia Therapeutics

Simon Delagrave

SVP

Ring Therapeutics

David Favre

CSO

InnoSkel

Jennifer Helfer

Senior Director, Patient Advocacy & Engagement

Encoded Therapeutics

Rajiv Gangurde

CTO

SparingVision

Xiaotong Fu

Senior Engineer

Biogen

Dawn Henke

Senior Scientific Program Manager

Standards Coordinating Body (SCB)

Eric Garr

Head of Process Development

FUJIFILM Diosynth Biotechnologies

John Jefferies

Professor and Chief, Division of Adult Cardiovascular Diseases

University of Tennessee Health Science Center

Vibha Jawa

Executive Director

Bristol Myers Squibb

Angela Johnson

Senior Director, Regulatory Strategy

Roivant

Bernard Kok

Senior Scientist

Poseida Therapeutics

Eric Kelsic

CEO

Dyno Therapeutics

Klaudia Kuranda

Head of Immunology

Spark Therapeutics

Emily Moran

Vice President of Vector Manufacturing

The Center for Breakthrough Medicines

Genevieve Laforet

VP, Clinical Development

BridgeBio Gene Therapy

Kei Kishimoto

CSO

Selecta Biosciences

Michael Ladd

VP, Regulatory Science

Orchard Therapeutics

Janet Lambert

CEO

ARM

Maryanne Maliwat

Director, Pricing, Reimbursement & Market Access

REGENXBIO

Nick Li

Senior Director, Global/US Market Access Lead

uniQure

Séverine Marconi

EU Senior Director, Regulatory Affairs

AskBio

Anju Mahesh

Senior Director, Regulatory CMC

Ultragenyx

Chris Mason

CSO

AVROBIO

Peter Marks

Director, CBER

FDA

Roel Gordijn

CCO

Polyplus-transfection

Becky Raymond

Senior Director of Business Development

Viralgen

Ganesh Krishnamoorthy, PhD

Senior Scientist, Downstream Process Development

Cytovance

Leslie Meltzer

CMO

Orchard Therapeutics

Sean McAuliffe

CCO

Taysha Gene Therapies

Amy Raymond

Senior Director of Therapeutic Expertise, Center for Rare Diseases

ICON

Emily McGinnis

Chief Patient Officer & Head of Government Affairs

Taysha Gene Therapies

Federico Mingozzi

CSO

Spark Therapeutics

Luca Alberici

GM, Milan CGT Center of Excellence

AGC Biologics

Amy Nicole Nayar

VP, US Patient Advocacy & Government Affairs

Novartis Gene Therapies

Asif Paker

VP, Clinical Development

SwanBio Therapeutics

Kara Langer

Senior Project Manager

Veristat LLC

Manish Muhuri

Instructor

University of Massachusetts Medical School

Christopher Park

Principal Analyst and Data Analytics Advisor

Medicaid & CHIP Payment & Access Commission (MACPAC)

Clark Paramore

Head of Value Demonstration, VP HEOR

bluebird bio

Hannah Jones

VP, Head of PBPK Consulting Services

Certara

Markus Peters

CEO

Aevitas Therapeutics

Alicia M. Baker McDowell, DRSc, MS

Head of Regulatory Strategy, Product Development & Market Access Consulting

Labcorp

Andre Singer

Biopharma Partnerships, Business Development Lead

Invitae

Jay Bryant-Wimp

VP, Patient Outcomes

Optum

Mo Heidaran, Ph.D.

Vice President – Technical, Regulatory & Access

Parexel

Kim Raineri

Chief Manufacturing & Technology Officer

AVROBIO

Mark Jones

Site Director Biologics

Charles River

Natalie Reash

Research Physical Therapist

Nationwide Children’s Hospital

Tori Schaefer, PhD

Director, Client Solutions – Life Sciences

Mix Talent

Abraham Scaria

CSO

AGTC

Jessica Riviere

VP, Global Patient Advocacy & Patient Engagement

Ultragenyx

Lisa Hoover

Associate Director, Cellular Assays

Precision for Medicine / Precision ADVANCE

Tayler Renshaw

Associate Director, Regulatory Affairs CMC

Astellas Gene Therapies

Lisa Stanek

VP, Translational Sciences

Affinia Therapeutics

Magali Taiel

CMO

GenSight Biologics

Mauricio Umana

Associate Director, Global Regulatory CMC Lead

Biogen

Michael Sherman

EVP & CMO

Point32 Health

Alexandra Watt

Module Manager, Advanced Therapies

Beacon Targeted Therapies

James Warren

VP, Pharmaceutical Development

Ultragenyx

Pierre-Axel Vinot

Associate Director, CMC Portfolio Management

SparingVision

Shaun Vigeant

Senior Director, Talent Acquisition & HRBP

Intellia Therapeutics

Brian Mosley

Scientist II, Analytical Science and Technology Lead CMC Analytical

BridgeBio Gene Therapy

Courtney Wells

VP, Clinical Operations & Clinical Affairs

Jaguar Gene Therapy

Genine Winslow

CEO

Chameleon Biosciences

Karl Whitney

VP, Regulatory Affairs

Precision Biosciences

Cathy Garabedian

Senior Director, New Product Planning

Keros Therapeutics

Dwayne Neal

Senior Director, Analytical Sciences

AVROBIO

Faraz Ali

CEO

Tenaya Therapeutics

Mariana Nacht

CSO

LogicBio

Brenda Faiola, Ph.D.

DABT, Senior Director, Nonclinical Development

Rho

Joseph Watson, Ph.D.

Associate Director Regulatory Strategy

Rho

Kaye Spratt

Chief Regulatory Officer

BridgeBio Gene Therapy

Lucas de Breed

Managing Director

August Care

Blair Miller

Principal

Trinity Life Sciences

Dylan Simon

Newborn Screening and Diagnostics Policy Manager

EveryLife Foundation for Rare Diseases

Erin Hulbert

Director

Optum

Kelsey Behrens, Ph.D.

Research Scientist

Rho

Beatriz Rocha MD, PhD

Vice President and Head, Global Regulatory Affairs and Product Development & Market Access Consulting

Labcorp

Bernardo Cordovez, Ph.D.

CSO and Co-Founder

Halo Labs

José Lora

Chief Scientific Officer

Intergalactic Therapeutics

Will Chou, MD.

CEO

Aruvant

Fred Porter

Chief Technical Office

Taysha Gene Therapies

Greg Gara

SVP of Manufacturing

Taysha Gene Therapies

Kim MacDonnell, BScN, MSc, RN, CGC

Lead Clinical Research Associate

Veristat LLC

Luman Wing, PhD

Vice President, Technical

Parexel International

Anshul Mangal

President

Precision ADVANCE & Project Farma

Joe Neroni

Director

Project Farma

Kelly Kilpatrick

Head of US Sales, Market Access & Operations

Spark Therapeutics

Tony Khoury

Executive Vice President

Project Farma

Jessica Ciccolella-Kahl

VP, Product Strategy

Accredo

Laura Hameed

Executive Director

Columbus Children’s Foundation

Louise Pacini

Chief Operating Officer

Vineti

Maximiliano F. Presa, Ph.D.

Study Director

The Jackson Laboratory

Kristin Heller, Ph.D.

Manager of Plasmid Production Facility

Andelyn Biosciences

Premdharan Meyyan

Senior Manager

Deallus

Rachel Reichman

Senior Consultant

Deallus

Ragho Chamkura

Senior Consultant

Deallus

Amy Price

Patient Advocate

Eric Crombez

Chief Medical Officer

Ultragenyx

Patrick Starremans, PhD

Director, Analytical Development

Resilience

Phil Cyr

SVP

Precision Value & Health / Precision ADVANCE

Conor Sullivan

Senior Talent Acquisition Manager

Dyno Therapeutics

Craig Martin

CEO

Global Genes

Palani Palaniappan

CTO, Pioneering Medicine

Flagship Pioneering

Peter Anastasiou

CEO

Capsida Biotherapeutics

Chris Fox

President

Novartis Gene Therapies

Kelley Miller

Senior Director, Managed Market

Optum

Phil Donenberg

CFO

Jaguar Gene Therapy

Yasser Kehail

Single Use & Enterprise Business Development Leader

Cytiva

Dale Moyer

Founder and President

Incentovate LLC

Dave Maheu

Senior Director, Pilot Plant & Technology Transfer

Ultragenyx

Kyle Bryant

Spokesperson

FARA (Friedreich’s Ataxia Research Alliance)

Sheila Mikhail

Chief Executive Officer & Co-Founder

AskBio

Amy Akillian

Head of Readiness & Optimization

Mix Talent

Debra Miller

Chief Executive Officer & Founder

CureDuchenne

Patty Adams

Head of Readiness & Optimization

Mix Talent