Speakers

Cristina Baricordi

Senior Scientist

AVROBIO

Deborah Ascheim

CMO

StrideBio

Eduard Ayuso

CTO

DiNAQOR

Luigi Barbarossa

Senior Research Associate

AVROBIO

Barbara Bonamassa ‘To be confirmed’

Quality Assessor

AIFA ‘To be confirmed’

Mike Byrne

Senior Director, Analytical Development & Product Quality

REGENXBIO

Ruth Castellanos

Associate Director

Stridebio

Ying Cai

Senior Director, Process Development

Ultragenyx

Daniel Chung

CMO

SparingVision

Fernanda Copeland

Executive Director, Global Head of Patient Advocacy & Engagement

AVROBIO

Jed Chatterton

VP, Gene Therapy

Gemini Therapeutics

Kent Christopherson

Senior Director, Medical Affairs

Orchard Therapeutics

Eric Faulkner

VP, Global RWE

Novartis Gene Therapies

Rebecca Derwin

Director, Early Commercial Strategy, Rare Programs

REGENXBIO

Scott Dorfman

CEO

Odylia Therapeutics

Simon Delagrave

SVP

Ring Therapeutics

David Favre

CSO

InnoSkel

Jennifer Helfer

Senior Director, Patient Advocacy & Engagement

Encoded Therapeutics

Rajiv Gangurde

CTO

SparingVision

Xiaotong Fu

Senior Engineer

Biogen

Bernard Kok

Senior Scientist

Poseida Therapeutics

Dawn Henke

Senior Scientific Program Manager

Standards Coordinating Body (SCB)

John Jefferies

Professor and Chief, Division of Adult Cardiovascular Diseases

University of Tennessee Health Science Center

Vibha Jawa

Executive Director

Bristol Myers Squibb

Angela Johnson

Senior Director, Regulatory Strategy

Roivant

Eric Kelsic

CEO

Dyno Therapeutics

Kei Kishimoto

CSO

Selecta Biosciences

Klaudia Kuranda

Head of Immunology

Spark Therapeutics

Genevieve Laforet

VP, Clinical Development

BridgeBio Gene Therapy

Janet Lambert

CEO

ARM

Kaye Spratt

Chief Regulatory Officer

BridgeBio Gene Therapy

Michael Ladd

VP, Regulatory Science

Orchard Therapeutics

Maryanne Maliwat

Director, Pricing, Reimbursement & Market Access

REGENXBIO

Nick Li

Senior Director, Global/US Market Access Lead

uniQure

Peter Marks

Director, CBER

FDA

Séverine Marconi

EU Senior Director, Regulatory Affairs

AskBio

Anju Mahesh

Senior Director, Regulatory CMC

Ultragenyx

Chris Mason

CSO

AVROBIO

Leslie Meltzer

CMO

Orchard Therapeutics

Sean McAuliffe

Chief Commercial Officer

Taysha Gene Therapies

Amy Nicole Nayar

VP, US Patient Advocacy & Government Affairs

Novartis Gene Therapies

Emily McGinnis

Chief Patient Officer & Head of Government Affairs

Taysha Gene Therapies

Federico Mingozzi

CSO

Spark Therapeutics

Manish Muhuri

Instructor

University of Massachusetts Medical School

Asif Paker

VP, Clinical Development

SwanBio Therapeutics

Christopher Park

Principal Analyst and Data Analytics Advisor

Medicaid & CHIP Payment & Access Commission (MACPAC)

Clark Paramore

Head of Value Demonstration, VP HEOR

bluebird bio

Will Chou, MD.

CEO

Aruvant

Kim Raineri

Chief Manufacturing & Technology Officer

AVROBIO

Markus Peters

CEO

Aevitas Therapeutics

Natalie Reash

Research Physical Therapist

Nationwide Children’s Hospital

Tayler Renshaw

Associate Director, Regulatory Affairs CMC

Astellas Gene Therapies

Abraham Scaria

CSO

AGTC

Jessica Riviere

VP, Global Patient Advocacy & Patient Engagement

Ultragenyx

Michael Sherman

EVP & CMO

Point32 Health

Sabah Sallah

SVP

Freeline Therapeutics

Lisa Stanek

VP, Translational Sciences

Affinia Therapeutics

Magali Taiel

CMO

GenSight Biologics

Mauricio Umana

Associate Director, Global Regulatory CMC Lead

Biogen

Shaun Vigeant

Senior Director, Talent Acquisition & HRBP

Intellia Therapeutics

Alexandra Watt

Module Manager, Advanced Therapies

Beacon Targeted Therapies

Courtney Wells

VP, Clinical Operations & Clinical Affairs

Jaguar Gene Therapy

James Warren

VP, Pharmaceutical Development

Ultragenyx

Pierre-Axel Vinot

Associate Director, CMC Portfolio Management

SparingVision

Eric Yearley

Associate Director, Analytical Development

BridgeBio Gene Therapy

Faraz Ali

CEO

Tenaya Therapeutics

Genine Winslow

CEO

Chameleon Biosciences

Karl Whitney

VP, Regulatory Affairs

Precision Biosciences

Cathy Garabedian

Senior Director, New Product Planning

Keros Therapeutics

Isabella Palazzolo

Associate Director, Regulatory CMC, Gene Therapy

Biogen

Lucas de Breed

Managing Director

August Care

Mariana Nacht

CSO

LogicBio

Brenda Faiola, Ph.D.

DABT, Senior Director, Nonclinical Development

Rho

Joseph Watson, Ph.D.

Associate Director Regulatory Strategy

Rho

Kelsey Behrens, Ph.D.

Research Scientist

Rho

Mo Heidaran, Ph.D.

Vice President – Technical, Regulatory & Access

Parexel

Andre Singer

Biopharma Partnerships, Business Development Lead

Invitae

Dylan Simon

Newborn Screening and Diagnostics Policy Manager

EveryLife Foundation for Rare Diseases

Ganesh Krishnamoorthy, PhD

Senior Scientist, Downstream Process Development

Cytovance

José Lora

Chief Scientific Officer

Intergalactic Therapeutics

Alicia M. Baker McDowell, DRSc, MS

Head of Regulatory Strategy, Product Development & Market Access Consulting

Labcorp

Beatriz Rocha MD, PhD

Vice President and Head, Global Regulatory Affairs and Product Development & Market Access Consulting

Labcorp

Bernardo Cordovez, Ph.D.

CSO and Co-Founder

Halo Labs

Krista Perry

Partner – Head of Launch Excellence

Trinity Life Sciences

Blair Miller

Principal

Trinity Life Sciences

Speaker to be Confirmed

Precision ADVANCE

Speaker to be Confirmed

Andelyn Biosciences

Speaker to be Confirmed

All Stripes Research

Speaker to be Confirmed

Project Farma

Speaker to be Confirmed

Charles River Laboratories

Speaker to be Confirmed

Center for Breakthrough Medicines

Speaker to be Confirmed

Optum Frontier