Panel Discussion: Breaking Boundaries: Navigating the Shift from Rare to Common Diseases in Gene Therapy
Time: 1:30 pm
day: Focus Day
Details:
• Exploring the unique challenges and benefits of expanding gene therapy into more prevalent conditions, including patient access, cost, and treatment scalability
• Evaluating the feasibility of widespread gene therapy applications in common diseases by 2025, along with realistic goals and potential hurdles
• Essential factors for successful translation, including regulatory preparedness, CMC adaptation, and the need for sustainable manufacturing and pricing models to meet higher demand
